Description
Center for Individualized Medicine Grand Rounds Series presents:
Advancing the Development of Gene Therapy for Rare Diseases
Genome editing holds great potential for disease treatment, prompting the FDA to update its approach to ensure these therapies are safe and effective and taking steps to help facilitate more efficient product development.
Join us for our Grand Rounds on October 10 at 12 p.m. CT. for Grand Rounds featuring Peter Marks, M.D., Ph.D., Director, Center for Biologics Evaluation and Research at the FDA. Dr. Marks will review approved gene therapies in the U.S., discuss genome editing technology for rare diseases, and describe platform technologies provisions' applicability to genome editing.